# Rescue of Infants With MCT8 Deficiency

> **NCT04143295** · — · AVAILABLE · sponsor: **Roy E. Weiss, M.D.**

## Conditions studied

- Mct8 (Slc16A2)-Specific Thyroid Hormone Cell Transporter Deficiency

## Interventions

- **DRUG:** Diiodothyropropionic acid (DITPA)

## Key facts

- **NCT ID:** NCT04143295
- **Lead sponsor:** Roy E. Weiss, M.D.
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** EXPANDED_ACCESS
- **Status:** AVAILABLE
- **Start date:** —
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2025-12-11


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04143295

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04143295, "Rescue of Infants With MCT8 Deficiency". Retrieved via AI Analytics 2026-06-26 from https://api.ai-analytics.org/clinical/NCT04143295. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*