Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
NCT04176523
·
clinicaltrials.gov ↗
RECRUITING
Status
95
Enrollment
INDUSTRY
Sponsor class
Conditions
Methylmalonic Acidemia
Propionic Acidemia
Interventions
DRUG:
Carglumic Acid
Sponsor
RECORDATI GROUP