A Long-term Follow-up Study in Participants Who Received CTX001
ENROLLING_BY_INVITATION
Status
Conditions
- Beta-Thalassemia
- Thalassemia
- Sickle Cell Disease
- Hematologic Diseases
- Hemoglobinopathies
- Genetic Diseases, Inborn
- Sickle Cell Anemia
Interventions
Sponsor
Vertex Pharmaceuticals Incorporated
Collaborators