Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures
Conditions
- Primary Immune Deficiency Disorder
- Immune Deficiency Disease
- Bone Marrow Failure
- Short Telomere Length
- Fanconi Anemia
- Non Fanconi DNA-DSB Repair Disorder
- Hoyeraal-Hreidarsson Syndrome
- Dyskeratosis Congenita
- Telomere Biology Disorder
- Short Telomere Syndrome
Interventions
- DRUG: Alemtuzumab
- DRUG: Fludarabine
- DRUG: Melphalan
- RADIATION: Low Dose Total Body Irradiation
- DRUG: Cyclophosphamide
- DRUG: Tacrolimus
- DRUG: Mycophenolate Mofetil
Sponsor
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Collaborators