Study to Evaluate the Efficacy and Safety of Valoctocogene Roxaparvovec, With Prophylactic Steroids in Hemophilia A
NCT04323098
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
22
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia A
Interventions
BIOLOGICAL:
valoctocogene roxaparvovec
Sponsor
BioMarin Pharmaceutical