Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia
Conditions
- Beta-Thalassemia
- Non-transfusion-dependent Thalassemia
Interventions
- DRUG: VIT-2763 once a day (QD)
- DRUG: VIT-2763 twice a day (BID)
- DRUG: Placebo
Sponsor
Vifor (International) Inc.
Collaborators