# Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome

> **NCT04400045** · PHASE2 · UNKNOWN · sponsor: **Federal Research Institute of Pediatric Hematology, Oncology and Immunology** · enrollment: 10 (estimated)

## Conditions studied

- Nijmegen Breakage Syndrome

## Interventions

- **DRUG:** Treosulfan

## Key facts

- **NCT ID:** NCT04400045
- **Lead sponsor:** Federal Research Institute of Pediatric Hematology, Oncology and Immunology
- **Sponsor class:** OTHER
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** UNKNOWN
- **Start date:** 2020-05-22
- **Primary completion:** 2023-05
- **Final completion:** 2023-05
- **Target enrollment:** 10 (ESTIMATED)
- **Last updated:** 2020-06-25


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04400045

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04400045, "Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome". Retrieved via AI Analytics 2026-06-24 from https://api.ai-analytics.org/clinical/NCT04400045. Licensed CC0.

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