# Characterization of the Clinical-epidemiological Profile of Patients With SMA5q Types II and III: Observational Study

> **NCT04404764** · — · COMPLETED · sponsor: **Hospital Israelita Albert Einstein** · enrollment: 155 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

- **DRUG:** Nusinersen Injectable Product

## Key facts

- **NCT ID:** NCT04404764
- **Lead sponsor:** Hospital Israelita Albert Einstein
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2020-05-27
- **Primary completion:** 2021-04-23
- **Final completion:** 2021-04-23
- **Target enrollment:** 155 (ACTUAL)
- **Last updated:** 2021-04-27

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04404764

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04404764, "Characterization of the Clinical-epidemiological Profile of Patients With SMA5q Types II and III: Observational Study". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT04404764. Licensed CC0.

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