Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2

NCT04470713 · clinicaltrials.gov ↗

COMPLETED

Status

226

Enrollment

INDUSTRY

Sponsor class

Conditions

GM1 Gangliosidosis
GM2 Gangliosidosis
Gaucher Disease, Type 2
Tay-Sachs Disease
AB Variant Gangliosidosis GM2
Sandhoff Disease

Sponsor

Idorsia Pharmaceuticals Ltd.