# TPO-Mimetic Use in Children for Hematopoietic Failure

> **NCT04478227** · EARLY_PHASE1 · COMPLETED · sponsor: **Anjali Sharathkumar** · enrollment: 15 (actual)

## Conditions studied

- Bone Marrow Failure Disorders
- Aplastic Anemia
- Thrombocytopenia
- Refractory Cytopenia of Childhood
- Myelodysplastic Syndrome(MDS)

## Interventions

- **DRUG:** Romiplostim

## Key facts

- **NCT ID:** NCT04478227
- **Lead sponsor:** Anjali Sharathkumar
- **Sponsor class:** OTHER
- **Phase:** EARLY_PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2020-08-18
- **Primary completion:** 2024-01-18
- **Final completion:** 2024-01-18
- **Target enrollment:** 15 (ACTUAL)
- **Last updated:** 2024-07-30

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04478227

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04478227, "TPO-Mimetic Use in Children for Hematopoietic Failure". Retrieved via AI Analytics 2026-05-31 from https://api.ai-analytics.org/clinical/NCT04478227. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
