# Natural History of Patients With Inherited Retinal Diseases Due to Mutations in RPE65 Gene

> **NCT04525261** · — · COMPLETED · sponsor: **University of Campania Luigi Vanvitelli** · enrollment: 60 (actual)

## Conditions studied

- Leber Congenital Amaurosis 2
- Retinitis Pigmentosa 20

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04525261
- **Lead sponsor:** University of Campania Luigi Vanvitelli
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2020-05-01
- **Primary completion:** 2020-07-31
- **Final completion:** 2020-07-31
- **Target enrollment:** 60 (ACTUAL)
- **Last updated:** 2023-11-29

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04525261

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04525261, "Natural History of Patients With Inherited Retinal Diseases Due to Mutations in RPE65 Gene". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT04525261. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
