A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis

NCT04525352 · clinicaltrials.gov ↗
PHASE1
Phase
TERMINATED
Status
1
Enrollment
INDUSTRY
Sponsor class

Stopped Study discontinued due to feasibility.

Conditions

Interventions

Sponsor

Rocket Pharmaceuticals Inc.

Collaborators