RGX-121 Gene Therapy in Children 5 Years of Age and Over With MPS II (Hunter Syndrome)
NCT04571970
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
6
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis Type II (MPS II)
Interventions
GENETIC:
RGX-121
Sponsor
REGENXBIO Inc.