# Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)

> **NCT04576494** · NA · COMPLETED · sponsor: **CHU de Reims** · enrollment: 4 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

- **OTHER:** Monthly assessments of functional motor abilities by a trained therapist
- **DRUG:** Nusinersen

## Key facts

- **NCT ID:** NCT04576494
- **Lead sponsor:** CHU de Reims
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2022-01-24
- **Primary completion:** 2023-01-24
- **Final completion:** 2023-09-08
- **Target enrollment:** 4 (ACTUAL)
- **Last updated:** 2024-12-04


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04576494

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04576494, "Study of the Functional Effects of Nusinersen in 5q-spinal Muscular Amyotrophy Adults (SMA Type 2 or 3 Forms)". Retrieved via AI Analytics 2026-07-20 from https://api.ai-analytics.org/clinical/NCT04576494. Licensed CC0.

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