# Registry Gangliosidoses

> **NCT04624789** · — · UNKNOWN · sponsor: **SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)** · enrollment: 40 (estimated)

## Conditions studied

- Gangliosidoses
- GM1 Gangliosidosis
- Morquio B Disease
- Sialidosis
- Galactosialidosis
- Gm2-Gangliosidosis, Variant B1
- Tay-Sachs Disease
- Sandhoff Disease
- GM2 Activator Deficiency

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04624789
- **Lead sponsor:** SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2020-06-08
- **Primary completion:** 2020-06-12
- **Final completion:** 2025-06-07
- **Target enrollment:** 40 (ESTIMATED)
- **Last updated:** 2020-11-12


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04624789

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04624789, "Registry Gangliosidoses". Retrieved via AI Analytics 2026-07-20 from https://api.ai-analytics.org/clinical/NCT04624789. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
