Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3
NCT04637282
·
clinicaltrials.gov ↗
PHASE3
Phase
NOT_YET_RECRUITING
Status
39
Enrollment
INDUSTRY
Sponsor class
Conditions
Juvenile Neuronal Ceroid Lipofuscinosis
Interventions
DRUG:
PLX-200
DRUG:
Placebo
Sponsor
Polaryx Therapeutics, Inc.