# Responsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen

> **NCT04644393** · — · UNKNOWN · sponsor: **Hospices Civils de Lyon** · enrollment: 40 (estimated)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04644393
- **Lead sponsor:** Hospices Civils de Lyon
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2020-11
- **Primary completion:** 2021-03
- **Final completion:** 2021-03
- **Target enrollment:** 40 (ESTIMATED)
- **Last updated:** 2020-11-25


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04644393

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04644393, "Responsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen". Retrieved via AI Analytics 2026-05-30 from https://api.ai-analytics.org/clinical/NCT04644393. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
