# Brain Involvement in Dystrophinopathies Part 2

> **NCT04668716** · — · COMPLETED · sponsor: **Great Ormond Street Hospital for Children NHS Foundation Trust** · enrollment: 339 (actual)

## Conditions studied

- Duchenne Muscular Dystrophy
- Becker Muscular Dystrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04668716
- **Lead sponsor:** Great Ormond Street Hospital for Children NHS Foundation Trust
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2021-10-11
- **Primary completion:** 2024-06-30
- **Final completion:** 2024-06-30
- **Target enrollment:** 339 (ACTUAL)
- **Last updated:** 2024-07-22

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04668716

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04668716, "Brain Involvement in Dystrophinopathies Part 2". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT04668716. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
