Acetazolamide Efficacy in Ataxia in PMM2-CDG
NCT04679389
·
clinicaltrials.gov ↗
PHASE2,PHASE3
Phase
TERMINATED
Status
25
Enrollment
OTHER
Sponsor class
Stopped
Lack of funding
Conditions
Pmm2-CDG
CDG1A
Interventions
DRUG:
Placebo
DRUG:
Acetazolamide
Sponsor
Mayo Clinic
Collaborators
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