Efficacy and Safety of Lomitapide in Paediatric Patients With Homozygous Familial Hypercholesterolaemia (HoFH)
NCT04681170
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
46
Enrollment
INDUSTRY
Sponsor class
Conditions
Homozygous Familial Hypercholesterolaemia (HoFH)
Interventions
DRUG:
Lomitapide
Sponsor
Amryt Pharma