Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients
NCT04690998
·
clinicaltrials.gov ↗
NA
Phase
ACTIVE_NOT_RECRUITING
Status
104
Enrollment
OTHER
Sponsor class
Conditions
Spinal Muscular Atrophy
Interventions
OTHER:
Blood Samples
OTHER:
MRI
Sponsor
Assistance Publique Hopitaux De Marseille