A Long-Term Safety Study of BCX9930 in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)
Stopped Sponsor decision
Conditions
- Paroxysmal Nocturnal Hemoglobinuria
- PNH
Interventions
- DRUG: BCX9930
- DRUG: Eculizumab
- DRUG: Ravulizumab
Sponsor
BioCryst Pharmaceuticals