Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis

NCT04713475 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

26

Enrollment

INDUSTRY

Sponsor class

Conditions

GM1 Gangliosidosis
GM1 Gangliosidosis, Type I
GM1 Gangliosidosis, Type 2
Beta-Galactosidase-1 (GLB1) Deficiency

Interventions

BIOLOGICAL: PBGM01

Sponsor

Gemma Biotherapeutics