FUSION: A Study to Evaluate the Efficacy, Safety, Pharmacokinetics and Pharmacodynamics of ION363 in Amyotrophic Lateral Sclerosis Participants With Fused in Sarcoma Mutations (FUS-ALS)
ACTIVE_NOT_RECRUITING
Status
Conditions
- Amyotrophic Lateral Sclerosis
Interventions
- DRUG: ION363
- DRUG: Placebo
Sponsor
Ionis Pharmaceuticals, Inc.