A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
ACTIVE_NOT_RECRUITING
Status
Conditions
- Transfusion-dependent Alpha-Thalassemia
- Transfusion-dependent Beta-Thalassemia
Interventions
- DRUG: Placebo Matching Mitapivat
- DRUG: Mitapivat
Sponsor
Agios Pharmaceuticals, Inc.