A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

NCT04770779 · clinicaltrials.gov ↗
PHASE3
Phase
ACTIVE_NOT_RECRUITING
Status
258
Enrollment
INDUSTRY
Sponsor class

Conditions

Interventions

Sponsor

Agios Pharmaceuticals, Inc.