Deoxynucleosides Pyrimidines as Treatment for Mitochondrial Depletion Syndrome
Conditions
- Mitochondrial Diseases
- Mitochondrial Encephalomyopathy
- Mitochondrial Encephalopathy
- Mitochondrial DNA Depletion
- Mitochondrial Metabolism Disorders
Interventions
- COMBINATION_PRODUCT: deoxycytidine and deoxythymidine
Sponsor
Kenneth Myers, MD