A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)

NCT04848779 · clinicaltrials.gov ↗

ACTIVE_NOT_RECRUITING

Status

16

Enrollment

INDUSTRY

Sponsor class

Conditions

Glycogen Storage Disease Type II

Interventions

DRUG: Alglucosidase alfa GZ419829

Sponsor

Sanofi