# A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)

> **NCT04848779** · — · ACTIVE_NOT_RECRUITING · sponsor: **Sanofi** · enrollment: 16 (estimated)

## Conditions studied

- Glycogen Storage Disease Type II

## Interventions

- **DRUG:** Alglucosidase alfa GZ419829

## Key facts

- **NCT ID:** NCT04848779
- **Lead sponsor:** Sanofi
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2021-06-10
- **Primary completion:** 2026-10-28
- **Final completion:** 2026-10-28
- **Target enrollment:** 16 (ESTIMATED)
- **Last updated:** 2025-05-13


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04848779

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04848779, "A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT04848779. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*