Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1
ACTIVE_NOT_RECRUITING
Status
Conditions
- Niemann-Pick Disease, Type C1
Interventions
- DRUG: Hydroxypropyl-beta-cyclodextrin
- DRUG: Placebo
Sponsor
Cyclo Therapeutics, Inc.