A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
NCT04901936
·
clinicaltrials.gov ↗
PHASE2
Phase
RECRUITING
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal Hemoglobinuria
Interventions
DRUG:
Pegcetacoplan
Sponsor
Apellis Pharmaceuticals, Inc.