# Natural History Observational Study of MPS IIIa in SMC

> **NCT04918641** · — · UNKNOWN · sponsor: **Samsung Medical Center** · enrollment: 25 (estimated)

## Conditions studied

- Sanfilippo Syndrome A

## Interventions

- **OTHER:** assessment

## Key facts

- **NCT ID:** NCT04918641
- **Lead sponsor:** Samsung Medical Center
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2021-06-30
- **Primary completion:** 2023-07-28
- **Final completion:** 2024-07-28
- **Target enrollment:** 25 (ESTIMATED)
- **Last updated:** 2021-06-09


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04918641

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04918641, "Natural History Observational Study of MPS IIIa in SMC". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT04918641. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
