# Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy

> **NCT04959890** · — · UNKNOWN · sponsor: **Fondazione Telethon** · enrollment: 15 (estimated)

## Conditions studied

- Severe Combined Immunodeficiency Due to ADA Deficiency

## Interventions

- **GENETIC:** Strimvelis

## Key facts

- **NCT ID:** NCT04959890
- **Lead sponsor:** Fondazione Telethon
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2021-04-23
- **Primary completion:** 2024-03-31
- **Final completion:** 2024-03-31
- **Target enrollment:** 15 (ESTIMATED)
- **Last updated:** 2024-01-29


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04959890

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04959890, "Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT04959890. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
