# Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008

> **NCT04995315** · — · COMPLETED · sponsor: **Agios Pharmaceuticals, Inc.** · enrollment: 13 (actual)

## Conditions studied

- Pyruvate Kinase Deficiency

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04995315
- **Lead sponsor:** Agios Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2021-07-02
- **Primary completion:** 2023-09-22
- **Final completion:** 2023-09-22
- **Target enrollment:** 13 (ACTUAL)
- **Last updated:** 2023-10-16


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04995315

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04995315, "Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT04995315. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
