A Study to Assess the Long-Term Safety and Efficacy of Eplontersen (Formerly Known as ION-682884, IONIS-TTR-LRx and AKCEA-TTR-LRx) in Patients With Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
ACTIVE_NOT_RECRUITING
Status
Conditions
- Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
Interventions
Sponsor
Ionis Pharmaceuticals, Inc.