BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants With Inadequate Response to C5 Inhibitor Therapy
Stopped Sponsor decision
Conditions
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
Interventions
- DRUG: Eculizumab
- DRUG: Ravulizumab
- DRUG: BCX9930
Sponsor
BioCryst Pharmaceuticals