BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants Not Receiving Other Complement Inhibitor Therapy
Stopped Sponsor decision
Conditions
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
Interventions
- DRUG: Placebo
- DRUG: BCX9930 monotherapy
Sponsor
BioCryst Pharmaceuticals