# A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

> **NCT05163288** · PHASE3 · RECRUITING · sponsor: **IntraBio Inc** · enrollment: 53 (estimated)

## Conditions studied

- Niemann-Pick Disease, Type C

## Interventions

- **DRUG:** N-Acetyl-L-Leucine
- **OTHER:** Placebo

## Key facts

- **NCT ID:** NCT05163288
- **Lead sponsor:** IntraBio Inc
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2022-06-30
- **Primary completion:** 2030-06-12
- **Final completion:** 2030-12
- **Target enrollment:** 53 (ESTIMATED)
- **Last updated:** 2026-04-03


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05163288

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05163288, "A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT05163288. Licensed CC0.

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