A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease
NCT05218655
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
101
Enrollment
INDUSTRY
Sponsor class
Conditions
Inherited Mitochondrial Disease
Interventions
DRUG:
Vatiquinone
Sponsor
PTC Therapeutics