# A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease

> **NCT05218655** · PHASE3 · COMPLETED · sponsor: **PTC Therapeutics** · enrollment: 101 (actual)

## Conditions studied

- Inherited Mitochondrial Disease

## Interventions

- **DRUG:** Vatiquinone

## Key facts

- **NCT ID:** NCT05218655
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2022-06-22
- **Primary completion:** 2025-04-15
- **Final completion:** 2025-04-15
- **Target enrollment:** 101 (ACTUAL)
- **Last updated:** 2025-12-22


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05218655

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05218655, "A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease". Retrieved via AI Analytics 2026-05-24 from https://api.ai-analytics.org/clinical/NCT05218655. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*