# ATA-100 (Formerly GNT0006) Gene Therapy Trial in Patients With LGMDR9

> **NCT05224505** · PHASE1 · ACTIVE_NOT_RECRUITING · sponsor: **Atamyo Therapeutics** · enrollment: 6 (actual)

## Conditions studied

- LGMDR9

## Interventions

- **BIOLOGICAL:** ATA-100 (AAV9 encoding FKRP gene)

## Key facts

- **NCT ID:** NCT05224505
- **Lead sponsor:** Atamyo Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2022-09-01
- **Primary completion:** 2025-02-01
- **Final completion:** 2029-09-30
- **Target enrollment:** 6 (ACTUAL)
- **Last updated:** 2025-10-06


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05224505

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05224505, "ATA-100 (Formerly GNT0006) Gene Therapy Trial in Patients With LGMDR9". Retrieved via AI Analytics 2026-07-27 from https://api.ai-analytics.org/clinical/NCT05224505. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*