# Gene Therapy Study for Children With CLN5 Batten Disease

> **NCT05228145** · PHASE1,PHASE2 · ACTIVE_NOT_RECRUITING · sponsor: **Neurogene Inc.** · enrollment: 6 (actual)

## Conditions studied

- Neuronal Ceroid Lipofuscinosis CLN5

## Interventions

- **GENETIC:** NGN-101

## Key facts

- **NCT ID:** NCT05228145
- **Lead sponsor:** Neurogene Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2022-01-31
- **Primary completion:** 2028-11
- **Final completion:** 2028-11
- **Target enrollment:** 6 (ACTUAL)
- **Last updated:** 2024-08-12


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05228145

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05228145, "Gene Therapy Study for Children With CLN5 Batten Disease". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT05228145. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*