# Research for Individualized Therapeutics in Rare Genetic Disease

> **NCT05236595** · — · ENROLLING_BY_INVITATION · sponsor: **Mayo Clinic** · enrollment: 50 (estimated)

## Conditions studied

- Rare Genetic Disease
- Undiagnosed Diseases

## Interventions

- **OTHER:** Individualized drug matching per genetic disease

## Key facts

- **NCT ID:** NCT05236595
- **Lead sponsor:** Mayo Clinic
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ENROLLING_BY_INVITATION
- **Start date:** 2021-11-24
- **Primary completion:** 2026-11
- **Final completion:** 2026-11
- **Target enrollment:** 50 (ESTIMATED)
- **Last updated:** 2026-01-20


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05236595

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05236595, "Research for Individualized Therapeutics in Rare Genetic Disease". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT05236595. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
