Safety and Efficacy of AMT-130 in European Adults With Early Manifest Huntington's Disease
NCT05243017
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
ACTIVE_NOT_RECRUITING
Status
14
Enrollment
INDUSTRY
Sponsor class
Conditions
Huntington Disease
Interventions
GENETIC:
intra-striatal rAAV5-miHTT
Sponsor
UniQure Biopharma B.V.