# Determine the Safety and Dose of EN001 in Patients With Charcot-Marie-Tooth Disease (CMT) Type 1A

> **NCT05333406** · PHASE1 · COMPLETED · sponsor: **ENCell** · enrollment: 9 (actual)

## Conditions studied

- Charcot-Marie-Tooth Disease, Type IA

## Interventions

- **DRUG:** EN001
- **DRUG:** EN001

## Key facts

- **NCT ID:** NCT05333406
- **Lead sponsor:** ENCell
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2022-02-22
- **Primary completion:** 2022-12-20
- **Final completion:** 2022-12-20
- **Target enrollment:** 9 (ACTUAL)
- **Last updated:** 2023-02-17


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05333406

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05333406, "Determine the Safety and Dose of EN001 in Patients With Charcot-Marie-Tooth Disease (CMT) Type 1A". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT05333406. Licensed CC0.

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