Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials

NCT05335876 · clinicaltrials.gov ↗

PHASE3

Phase

RECRUITING

Status

175

Enrollment

INDUSTRY

Sponsor class

Conditions

Spinal Muscular Atrophy (SMA)

Interventions

BIOLOGICAL: onasemnogene abeparvovec

Sponsor

Novartis Pharmaceuticals