Pharmacodynamic EffIcacy and Clinical Benefit of AT 007 in Patients With Sorbitol Dehydrogenase (SORD) Deficiency
ACTIVE_NOT_RECRUITING
Status
Conditions
- Hereditary Neuropathy Caused by SORD Deficiency
Interventions
- DRUG: AT-007
- DRUG: Placebo
Sponsor
Applied Therapeutics, Inc.