Evaluating the Efficacy and Safety of D-galactose in PGM1-CDG (AVTX-801)
NCT05402332
·
clinicaltrials.gov ↗
PHASE2
Phase
NOT_YET_RECRUITING
Status
8
Enrollment
OTHER
Sponsor class
Conditions
PGM1-CDG - Phosphoglucomutase 1-Related Congenital Disorder of Glycosylation
Interventions
DRUG:
AVTX-801
DRUG:
Placebo
Sponsor
Eva Morava-Kozicz
Collaborators
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