# ERT in Pompe Disease: Elucidation of Molecular Structures Contributing to Enzyme Uptake and Immunoreactivity

> **NCT05448131** · — · UNKNOWN · sponsor: **Centre for Analytical Biochemistry and Biomedical Mass Spectrometry** · enrollment: 50 (estimated)

## Conditions studied

- Pompe-Disease

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05448131
- **Lead sponsor:** Centre for Analytical Biochemistry and Biomedical Mass Spectrometry
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2023-02-01
- **Primary completion:** 2024-08-06
- **Final completion:** 2024-10-07
- **Target enrollment:** 50 (ESTIMATED)
- **Last updated:** 2023-02-21

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05448131

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05448131, "ERT in Pompe Disease: Elucidation of Molecular Structures Contributing to Enzyme Uptake and Immunoreactivity". Retrieved via AI Analytics 2026-05-23 from https://api.ai-analytics.org/clinical/NCT05448131. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
