A Study of FVIII Gene Therapy for Hemophilia A
NCT05454774
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
RECRUITING
Status
8
Enrollment
OTHER
Sponsor class
Conditions
Hemophilia A
Interventions
GENETIC:
Single dose intravenous injection of BBM 002
Sponsor
Institute of Hematology & Blood Diseases Hospital, China