# Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America

> **NCT05475691** · — · UNKNOWN · sponsor: **Hospital Israelita Albert Einstein** · enrollment: 361 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05475691
- **Lead sponsor:** Hospital Israelita Albert Einstein
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2022-08-17
- **Primary completion:** 2024-08-30
- **Final completion:** 2025-01-30
- **Target enrollment:** 361 (ACTUAL)
- **Last updated:** 2024-03-08

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05475691

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05475691, "Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT05475691. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
